Tagged: rare diseases

CPT Rare Diseases Call for Papers

May 13, 2024

Clinical Pharmacology & Therapeutics has an open call for papers on Rare and Orphan Diseases, but the deadline is closing soon! Check out the latest episode of ClinPharmPod, where Editors-in-Training Drs. Mai Mehanna and Ya-Feng (Jay) Wen detail why CPT chose this theme and what types of papers the editors are hoping to receive. If you have questions about submitting papers for this themed issue, please contact Managing Editor Aletha Gerding at [email protected].

ClinPharmPod

CPT Rare Diseases Call for Papers

00:00 / 12:03

Sharing Data to Improve Patient-Focused Outcomes

April 26, 2022

Critical Path Institute’s Dr. Diane Stephenson joins host Alaina Webster to discuss the importance of data sharing to improve patient care, particularly in Neuroscience. Diane and her co-authors recently published a Review, “Can Innovative Trial Designs in Orphan Diseases Drive Advancement of Treatments for Common Neurological Diseases?”, in the April Neuroscience-themed issue of Clinical Pharmacology & Therapeutics, and she ties this work into successful data sharing models and their impact on patient outcomes. Critical Path Institute has accumulated more than 300 clinical data studies across 15+ disease areas, and its repository of data currently includes information on the following neuroscience diseases: Alzheimer’s disease, Huntington’s disease, ataxias, Duchenne muscular dystrophy, Parkinson’s disease, and multiple sclerosis.

ClinPharmPod

Sharing Data to Improve Patient-Focused Outcomes

00:00 / 14:50

What’s New in Neuroscience?

March 19, 2022

Clinical Pharmacology & Therapeutics recently published its second themed issue of 2022 – Therapeutics in Neuroscience. Join Editor-in-Chief Dr. Piet van der Graaf and Associate/Guest Editors Drs. Spiros Vamvakas, Paulien Ravenstijn, and Iris Minichmayr as they delve into reasons for the theme, what papers caught their eyes, and what action items they hope to leave with readers. If you’re interested in submitting your research for any upcoming themed issues in ASCPT’s Journal Family, you can find Calls for Papers and more information here.

ClinPharmPod

What’s New in Neuroscience?

00:00 / 13:07

Marlene Haffner on Orphan Drugs

November 28, 2016

This episode features Marlene Haffner, MD, MPH of Haffner Associates, LLC discussing orphan drug regulation in the United States and beyond. Read her article which published in the October 2016 issue here.

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ClinPharmPod

Marlene Haffner on Orphan Drugs

00:00 / 19:50